Columnist Shalom Lim describes a moving performance at the Enabling Lives Festival in Singapore, an example of the power of ...

Sarepta has acquired the global rights to develop ARO-DUX4 and ARO-DM1, two RNAi therapeutic candidates for types of muscular ...

The case is reported of a young woman who began having DMD symptoms before getting pregnant, allowing her to receive genetic ...

Columnist Robin Stemple knows his walker should help prevent falls, but it didn't work out that way on a simple maneuver to ...

Based on the positive findings from the Phase 1/2 study, Genethon is planning to launch Phase 3 testing of GNT0004 next year.

Regenxbio has initiated the pivotal phase of a clinical trial testing its experimental gene therapy RGX-202 in boys with ...

Couch shopping made columnist Betty Vertin discover she was focused on her three children with DMD rather than the rest of her family.

Columnist Patrick Moeschen, who lives with limb-girdle muscular dystrophy, explains why controlling what he can is so ...