CRISPR gene therapy Casgevy can nearly eliminate sickle cell crises, but difficult stem‑cell collection is delaying access ...

“It can hit you out of nowhere,” she tells TODAY.com.

As Uganda rolls out mandatory nationwide screening of newborns for sickle cell disease this month, a gene therapy celebrated ...

As Uganda rolls out mandatory nationwide screening of newborns for sickle cell disease this month, a gene therapy celebrated in the United States and Europe remains financially out of reach for most ...

The first gene therapies approved to treat sickle cell disease in December 2023 are struggling on the market. But there are ...

While African governments expand basic treatment, high-income countries adopt the first gene-editing therapy to cure sickle cell.

Mean absolute fetal hemoglobin (HbF) increased by 12.2% (from 7.1% to 19.3%) at Week 12 (n=12), representing a rapid, robust, and clinically ...

You Look Fine” is a groundbreaking new documentary, offering an intimate, first-person account of living with sickle cell disease.

This article is part of a Rare Disease series sponsored by DeepIntent. With Rare Disease Month wrapping up and Rare Disease Day taking place on Saturday, MM+M is celebrating a handful of campaigns ...

Researchers found higher C-reactive protein levels during the follicular phase in women with sickle cell disease, indicating cycle-linked inflammation shifts.

Pain related to sickle cell disease (SCD) increases during menstruation, as do emergency department (ED) visits and hospitalizations, for many women and girls - according to a new, nationwide ...