Stoke Therapeutics (NASDAQ:STOK) used its presentation at the Guggenheim Emerging Outlook Biotech Summit 2026 to highlight ...

PsychoGenics has signed on with Italy's Iama Therapeutics to run a preclinical study as part of an effort to identify and develop drug candidates to treat Dravet syndrome. Under the agreement, the U.S ...

– New data include 24-month results from the largest and longest prospective natural history study of children and adolescents with Dravet syndrome, which showed a lack of improvement despite ...

Even when promising clinical trials exist, and the FDA allows expanded access, rare disease patients like my granddaughter ...

Most parents worry about scraped knees, tumbles on the playground or gym class injuries. But for the Raia and Tisdale families, their everyday fears are life-threatening: a seizure that can strike ...

The Dravet syndrome community is invited to share videos highlighting the sounds of their everyday life with fewer seizures on FINTEPLA ® (fenfluramine). The project will display a gallery of videos ...

A Takeda Pharmaceutical drug in development for rare forms of epilepsy that are resistant to anti-seizure medications has failed to meet the main goals of two placebo-controlled pivotal studies, a ...

In the wake of a market pull in obesity nearly five years ago, the other shoe has dropped for Eisai’s serotonin 2C receptor agonist lorcaserin. Eisai has formally terminated a phase 3 study of ...

Stoke Therapeutics' TANGO platform enhances RNA output to compensate for gene mutations causing severe genetic diseases. STOK primarily focuses on developing treatments for Dravet syndrome and ...

After raising $52,000 with a 5K last year to fund research into their son’s rare seizure disorder, Matthew and Reagan Hill hope for similar success at “Cael’s Climb” at McDade Park on Sunday. Cael ...

LACKAWANNA COUNTY, Pa. — Seven-year-old Cael Hill of Roaring Brook just started kindergarten this year. "He is very into dinosaurs and Spider-Man. Your typical little boy in terms of his interests, ...

ST. LOUIS — The 7th Annual Dance for Dravet is just around the corner, taking place on September 26th at the Third Degree Glass Factory. Hosted by the Brennan family in honor of 8-year-old Anna Odlaug ...